Vieira, Paula Manuel, Cristina Garrido, and Manuela Santos. “Presymptomatic Treatment of Type 1 Spinal Muscular Atrophy – A Literature Review”. NASCER E CRESCER - BIRTH AND GROWTH MEDICAL JOURNAL 32, no. 4 (January 23, 2024): 299–305. Accessed February 6, 2025. https://revistas.rcaap.pt/nascercrescer/article/view/28929.